June 21 marks World ALS Awareness Day, a global moment to spotlight the fight against this relentless neurodegenerative disease. With no cure yet, recent tech-driven breakthroughs are lighting new paths for treatment—and they’re as futuristic as they sound!
An international team including researchers from Tsinghua University, Harvard, and AI drug-discovery firm Insilico Medicine used PandaOmics, an AI platform, to uncover 28 new therapeutic targets for ALS. In animal tests, suppressing eight of these genes slashed neurodegeneration—a win for AI’s role in speeding up drug discovery!
Meanwhile, scientists at CUHK and Oxford cracked another piece of the ALS puzzle: a disrupted protein called YY1 that triggers motor neuron death. ‘This opens doors for smarter drug designs,’ said CUHK’s Prof. Edwin Chan. Their findings, published in Nature Communications, could reshape how we tackle ALS at the molecular level.
And here’s the kicker: Chinese biotech firm SineuGene Therapeutics just completed trials for a gene therapy drug targeting ALS. CEO Peng Lin called it a ‘global milestone,’ developed in just two years using Tsinghua University’s neuroscience research.
From AI to gene editing, science is turning the tide against ALS. This Awareness Day isn’t just about spreading knowledge—it’s about celebrating the brains behind the breakthroughs. Let’s keep the momentum going!
Reference(s):
cgtn.com